Skip to content

Exposure to US cancer drugs with lack of confirmed benefit after US Food and Drug Administration accelerated approval

Published

February 2023

Citation

Parikh RB, Hubbard RA, Wang E, et al. Exposure to US Cancer Drugs With Lack of Confirmed Benefit After US Food and Drug Administration Accelerated Approval. JAMA Oncol. (2023) https://doi.org/10.1001/jamaoncol.2022.7770

Our summary

From 2009 to 2022, the FDA approved 65 malignant hematology and oncology treatments under the Accelerated Approval (AA) program. After approval, these drugs must show clinical benefits (such as longer progression-free survival or overall survival). However, since 2009, 15 (23%) of these approvals have been withdrawn due to a lack of demonstrated benefit.

In this study, researchers calculated the percentage of patients exposed to oncology drugs later withdrawn due to a lack of confirmed benefit following AA approval.

Why this matters

With the growing number of cancer therapies being granted AA and the increasing number of FDA withdrawals due to negative post-approval trials, it is crucial to strike a balance between providing timely access to cancer therapies and maintaining high standards of safety and efficacy for patients.

Read the research

Share